Active Pharmaceutical Ingredient (API)
Elivaldogene Autotemcel
Gene Therapy (Adrenoleukodystrophy)
A one-time ex vivo gene therapy for early active cerebral adrenoleukodystrophy ($\text{CALD}$). It involves transplanting the patient's own CD34+ cells which have been modified to express the missing ABCD1 protein.
Technical Profile
- Reference Code
- ELI827
- CAS Number
- N/A
- Chemical Class
- N/A
- Therapeutic Class
- N/A
Verified Brands
Medicines containing Elivaldogene Autotemcel as an active ingredient.
| Brand Name | Manufacturer | Formulation | MRP | |
|---|---|---|---|---|
| No verified brands found for this salt. | ||||